Leadership team
Shaping the future of rare disease
We don’t just work for a company; we work for a cause. Our mission has led us to bring a spirit of innovation to every aspect of the drug development process. From discovery, to the design of our clinical trials, our deep passion for patients drives us to urgently seek ways to do things differently.
Meet our executive leadership
This inspiring group of innovators and big thinkers are changing the face of treatments for rare diseases — all for the good of patients and their families.
